This is what gene therapy can do in 2026. | Svetlana Repnitskaya/Getty Images
In a lab room, a toddler, deaf from birth, sits while a tone plays. There’s no reaction. His face does not change.
Six weeks later, after a single injection of an experimental gene therapy, the same toddler is back in the same room. The tone plays. The toddler’s head turns toward the sound. And somewhere just off screen, the child’s grandfather says his name. The boy turns and looks. He can hear.
“When the parents realized their child had a response to sound they cried,” says Dr. Yilai Shu of the Eye &...
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